PRECLINICAL
PHASE 1
PHASE 2
PHASE 3
PRE
P1
P2
P3
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Updated: 04/02/2025

Pipeline Type

New Drugs in Development

Phase Of Development

Phase 1

Sponsors and Collaborators

uniQure

Mechanism of Action

Gene Therapy
Glutamate
New Route of Administration

Mechanism Description

Populations Tested In

N/A

Special FDA Designation

None

Nonprofit or Government Support

N/A

Nonprofit or Government Support Description

Previous Presentations

Location of Clinical Trials

California Locations
Palo Alto, California, United States, 94304
Recruiting

Stanford University
Contact: Jordan Seliger
650-460-9260 jseliger@stanford.edu
Contact: Yi Li, MD, PhD

Maryland Locations
Baltimore, Maryland, United States, 21287
Recruiting

Johns Hopkins School of Medicine
Contact: Joon Kang, MD
410-955-2822 Jkang50@jh.edu
Contact: Joon Kang, MD
Bethesda, Maryland, United States, 20817
Recruiting

Midatlantic Epilepsy and Sleep Center
Contact: Pavel Klein, M.D.
301-530-9744 kleinp@epilepsydc.com
Contact: Pavel Klein, M.D.

Massachusetts Locations
Boston, Massachusetts, United States, 02114
Recruiting

Massachusetts General Hospital
Contact: Erin Donahue
617.643.3732 ekdonahue@mgh.harvard.edu
Contact: Mark Richardson, MD, PhD
Boston, Massachusetts, United States, 02115
Recruiting

Brigham and Women's Hospital
Contact: Kathy Vernovsky
857-282-5172 kvernovsky@mgb.org
Contact: Ellen Bubrick, MD

Michigan Locations
Grand Rapids, Michigan, United States, 49503
Recruiting

Corewell Health
Contact:
David Burdette, MD
(616) 267-0301 david.burdette@corewellhealth.org
Contact:
David Burdette, MD

New Hampshire Locations
Lebanon, New Hampshire, United States, 03756
Recruiting

Dartmouth Hitchcock Medical Center
Contact: Anastasia Kanishcheva, MPH, CCRC
603-650-0260 Anastasia.Kanishcheva@Hitchcock.ORG
Contact: Barbara Jobst, MD

New Jersey Locations
Hackensack, New Jersey, United States, 07601
Recruiting

Northeast Regional Epilepsy Group
Contact: Hardik Rana
551-497-5000 hrana@epilepsygroup.com
Contact: Asfi Rafiuddin
New Brunswick, New Jersey, United States, 08901
Recruiting

Robert Wood Johnson Hospital
Contact: Sheila Redding
732-235-6121 sr1238@rwjms.rutgers.edu
Contact: Robert E Gross, MD, PhD

Ohio Locations
Cleveland, Ohio, United States, 44195
Recruiting

Cleveland Clinic
Contact: Xiaoming Zhang
216-445-7510 zhangx6@ccf.org
Contact: Imad Najm, MD
Columbus, Ohio, United States, 43210
Recruiting

Ohio State University
Contact: Elizabeth Wiley
614-293-3660 Elizabeth.Wiley@osumc.edu
Contact: Timothy Lucas, MD, PHD

Pennsylvania Locations
Philadelphia, Pennsylvania, United States, 19104
Recruiting

Hospital of the University of Pennsylvania
Contact: Melissa Johnston Esparza, MS
215-614-0520 melissa.johnstonesparza@pennmedicine.upenn.edu
Contact: Michael Gelfand, MD, PhD

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